A University of California, San Francisco (UCSF) new protocol has successfully treated a fetus with a devastating genetic disorder for the first time. This gives hope to unborn people who have rare genetic illnesses.
The plan has been used to help people with Hunter Syndrome and other lysosomal storage diseases.
Women who are pregnant and whose unborn children have been diagnosed with these diseases have come to UCSF to take part in the study.
The study is a big step forward in the history of fetal therapy, which has grown from surgery to treat physical problems to medical treatments for genetic problems.
Fetal treatment is an exciting field that could help people who are still in the womb who have rare genetic diseases.
A new CRISPR lab has been set up to give people who have rare and deadly genetic diseases hope for treatments that can cure them. The center’s goal is to use CRISPR technology to find new ways to treat genetic diseases that can’t be treated now.
The work of the center is part of a larger effort to protect gene therapies for rare diseases, which are in danger because they are expensive to make and only help a few people.
There is hope and support for families who have been diagnosed with fetal syndrome through groups like the Fetal Health Foundation. This non-profit was started by parents and gives families information and tools.
The foundation’s goal is to help families make smart choices about their care and put them in touch with treatment centers that can give their future child the best care.
Finally, fetal therapy gives hope to people who are still in the womb and have rare genetic illnesses. Hunter Syndrome is one of the lysosomal storage diseases that the procedure created at UCSF has shown promise in treating.
The opening of a new CRISPR lab and the work of groups like the Fetal Health Foundation give families who have been diagnosed with fetal syndrome more hope. These changes show that fetal therapy has a lot of promise for treating rare genetic diseases in people who are still in the womb.